Global Duchenne Muscular Dystrophy Treatment Market: Key Developments
In April 2022, Pfizer Inc. planned to open the first U.S. sites in the Phase III study evaluating the investigational mini-dystrophin gene therapy, fordadistrogene movaparvovec, in ambulatory patients with Duchenne muscular dystrophy.
In February 2021, Sarepta Therapeutics, Inc. announced that the U.S. Food & Drug Administration (FDA) has approved AMONDYS 45 (casimersen). AMONDYS 45 is an antisense oligonucleotide from the Sarepta’s phosphorodiamidate morpholino oligomer (PMO) platform, for the treatment of DMD in patients with a confirmed mutation amenable to exon 45 skipping.
In February 2021, the District Attorney (DA) of the United States approved Sarepta Therapeutics' Amondys 45 (casimersen injectable), an antisense oligonucleotide for the treatment of people with Duchenne Muscular Dystrophy.
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