CELL AND GENE THERAPY MARKET ANALYSIS

Leading Companies

Global Cell and Gene Therapy Market- Key Players

• Major players operating in the global cell and gene therapy market include Novartis International AG, Pfizer, Inc., Sanofi S.A., Amgen, Inc., Regeneron Pharmaceuticals, Inc., Bluebird Bio, Inc. (Celgene Corporation), Biogen Inc., uniQure N.V., JCR Pharmaceuticals Co. Ltd., Gene Biotherapeutics, Kolon TissueGene, Inc., Horama S.A., MeiraGTx Limited, Gilead Sciences, Inc., Organogenesis, Inc., Orchard Therapeutics Plc., Freeline Therapeutics Ltd., Bristol-Myers Squibb Company, PTC Therapeutics, Inc., Spark Therapeutics, Inc., and Biomarin Pharmaceutical Inc.

*Definition: Stem cell therapy (SCT) involves the treatment of various disorders ranging from non-serious to life-threatening diseases by using stem cells. Stem cells are used to potentially treat more than 80 disorders, including neuromuscular and degenerative disorders. Gene therapy is an approach to treat genetic diseases by augmenting, replacing, or suppressing the mutated genes with functional copies. They address the root cause of an inherited disease by enabling the body to produce necessary proteins and restore normal functioning. Gene therapy involves the transfer of genetic material through a suitable carrier or vector.