Table of Content - Hemoglobinopathy Treatment Drugs Market

The hemoglobinopathies encompass all genetic diseases of hemoglobin. They fall into two main groups: thalassemia syndromes and structural hemoglobin variants (abnormal hemoglobins). α and β thalassemia are the main types of thalassemia; the main structural hemoglobin variants are HbS, HbE, and HbC. There are many subtypes and combined types in each group. The highly variable clinical manifestations of the hemoglobinopathies range from mild hypochromic anemia to moderate hematological disease to severe, lifelong, transfusion-dependent anemia with multiorgan involvement. Stem-cell transplantation is the preferred treatment for severe forms of thalassemia. Supportive, rather than curative, treatment consists of periodic blood transfusions for life combined with iron chelation. Drugs to treat the symptoms of sickle-cell disease include analgesics, antibiotics, ACE inhibitors, and hydroxyurea. Blood transfusions should be given only when strictly indicated. More than 90% of patients currently survive into adulthood. Optimally treated patients have a projected life span of 50 to 60 years. With approximately 7% of the worldwide population being carriers, hemoglobinopathies are the most common monogenic diseases and one of the world’s major health problems. They were originally found mainly in the Mediterranean area and large parts of Asia and Africa. International migration has spread them from those areas all over the world. In many parts of Europe today, hemoglobin (Hb) defects are classified as endemic diseases.

Market Dynamics

Increasing launches of new products and mergers and acquisitions by key market players are expected to drive the global hemoglobinopathy treatment drugs market growth. For instance, on August 8, 2022, Pfizer Inc., a U.S.-based multinational pharmaceutical and biotechnology corporation, and Global Blood Therapeutics, Inc., a U.S.-based Healthcare company, announced that the companies have entered into a definitive agreement under which Pfizer will acquire GBT. Under the terms of the transaction, Pfizer Inc will acquire all the outstanding shares of Global Blood Therapeutics, Inc. for US$ 68.50 per share in cash, for a total enterprise value of approximately US$ 5.4 billion, including debt and net of cash acquired. The Boards of Directors of both companies have unanimously approved the transaction.

Key features of the study:

This report provides an in-depth analysis of the global hemoglobinopathy treatment drugs market and provides market size (US$ Billion) and compound annual growth rate (CAGR) for the forecast period (2023–2030), considering 2022 as the base year
It elucidates potential revenue opportunities across different segments and explains attractive investment proposition matrices for this market
This study also provides key insights about market drivers, restraints, opportunities, new product launches or approval, market trends, regional outlook, and competitive strategies adopted by key players
It profiles key players in the global hemoglobinopathy treatment drugs market based on the following parameters– company highlights, products portfolio, key highlights, financial performance, and strategies
Key companies covered as a part of this study include Bristol-Myers Squibb Company, GlycoMimetics Inc., Pfizer Inc., Anthera Pharmaceuticals Inc., Eli Lilly and Company, Mast Therapeutics, Daiichi Sankyo Company Ltd., Novartis International AG, Bluebird Bio Inc., HemaQuest Pharmaceuticals Inc., Emmaus Medical Inc., Baxter International Inc., Prolong Pharmaceuticals, Medunik USA Inc., Sangamo Therapeutics, Inc., Global Blood Therapeutics, Alnylam Pharmaceuticals, and Acceleron Pharma, Inc.
Global hemoglobinopathy treatment drugs market report caters to various stakeholders in this industry including investors, suppliers, product manufacturers, distributors, new entrants, and financial analysts
Stakeholders would have ease in decision-making through various strategy matrices used in analyzing the global hemoglobinopathy treatment drugs market

Detailed Segmentation:

Global Hemoglobinopathy Treatment Drugs Market, By Drug Type:
- Analgesics
- Antibiotics
- ACE Inhibitors
- Hydroxyurea
- Others
Global Hemoglobinopathy Treatment Drugs Market, By Disease Type:
- Thalassemia
- Sickle Cell Disease
- Other Hb Variants Diseases
Global Hemoglobinopathy Treatment Drugs Market, By Distribution Channel:
- Hospitals Pharmacies
- Retail Pharmacies
- Online Pharmacies
Global Hemoglobinopathy Treatment Drugs Market, By Region:
- North America
  - U.S.
  - Canada
- Europe
  - U.K.
  - Germany
  - Italy
  - Spain
  - France
  - Russia
  - Rest of Europe
- Asia Pacific
  - Australia
  - India
  - China
  - Japan
  - ASEAN
  - South Korea
  - Rest of Asia Pacific
- Latin America
  - Brazil
  - Mexico
  - Argentina
- Middle East
  - GCC Countries
  - Israel
  - Rest of Middle East
- Africa
  - South Africa
  - Central Africa
  - North Africa
Company Profiles
- Bristol-Myers Squibb Company
- GlycoMimetics Inc.
- Pfizer Inc.
- Anthera Pharmaceuticals Inc.
- Eli Lilly and Company
- Mast Therapeutics
- Daiichi Sankyo Company Ltd.
- Novartis International AG
- Bluebird Bio Inc.
- HemaQuest Pharmaceuticals Inc.
- Emmaus Medical Inc.
- Baxter International Inc.
- Prolong Pharmaceuticals
- Medunik USA Inc.
- Sangamo Therapeutics, Inc.
- Global Blood Therapeutics, Inc.
- Alnylam Pharmaceuticals
- Acceleron Pharma, Inc.

Table of Contents

Research Objectives and Assumptions
- Research Objectives
- Assumptions
- Abbreviations
Market Purview
- Report Description
  - Market Definition and Scope
- Executive Summary
  - Market Snapshot, By Drug Type
  - Market Snapshot, By Disease Type
  - Market Snapshot, By Distribution Channel
  - Market Snapshot, By Region
- Coherent Opportunity Map (COM)
Market Dynamics, Regulations, and Trends Analysis
- Market Dynamics
  - Drivers
  - Restraints
  - Market Opportunities
- Impact Analysis
- Recent Product Launches
- Epidemiology
- Merger, Acquisition, and Collaborations
- Regulatory Scenario
- Key Developments
- PEST Analysis
Global Hemoglobinopathy Treatment Drugs Market– COVID-19 Impact Analysis
- Economic Impact
- COVID-19 Epidemiology
- Impact on Supply and Demand
Global Hemoglobinopathy Treatment Drugs Market, By Drug Type, 2018–2030, (US$ Billion)
- Introduction
  - Market Share Analysis, 2023 and 2030 (%)
  - Y-o-Y Growth Analysis, 2018–2030
  - Segment Trends
- Analgesics
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
- Antibiotics
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
- ACE Inhibitors
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
- Hydroxyurea
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
- Others
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Global Hemoglobinopathy Treatment Drugs Market, By Disease Type, 2018–2030, (US$ Billion)
- Introduction
  - Market Share Analysis, 2023 and 2030 (%)
  - Y-o-Y Growth Analysis, 2018–2030
  - Segment Trends
- Thalassemia
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
- Sickle Cell Disease
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
- Other Hb Variants Diseases
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Global Hemoglobinopathy Treatment Drugs Market, By Distribution Channel, 2018–2030, (US$ Billion)
- Introduction
  - Market Share Analysis, 2023 and 2030 (%)
  - Y-o-Y Growth Analysis, 2018–2030
  - Segment Trends
- Hospitals Pharmacies
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
- Retail Pharmacies
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
- Online Pharmacies
  - Introduction
  - Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Global Hemoglobinopathy Treatment Drugs Market, By Region, 2018–2030, (US$ Billion)
- Introduction
  - Market Share Analysis, By Region, 2023 and 2030 (%)
  - Y-o-Y Growth Analysis, For Region, 2018–2030
- Regional Trends
  - North America
    - Introduction
    - Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
      - U.S.
      - Canada
  - Latin America
    - Introduction
    - Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
      - Brazil
      - Mexico
      - Argentina
      - Rest of Latin America
  - Europe
    - Introduction
    - Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
      - U.K.
      - Germany
      - Italy
      - France
      - Spain
      - Russia
      - Rest of Europe
  - Asia Pacific
    - Introduction
    - Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
      - China
      - India
      - Japan
      - ASEAN
      - Australia
      - South Korea
      - Rest of Asia Pacific
  - Middle East
    - Introduction
    - Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
      - GCC
      - Israel
      - Rest of Middle East
  - Africa
    - Introduction
    - Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
    - Market Size and Forecast, and Y-o-Y Growth, By Country/Sub-region, 2018–2030, (US$ Billion)
      - North Africa
      - Central Africa
      - South Africa
Competitive Landscape
- Bristol-Myers Squibb Company
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- GlycoMimetics Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Pfizer Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Anthera Pharmaceuticals Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Eli Lilly and Company
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Mast Therapeutics
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Daiichi Sankyo Company Ltd.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Novartis International AG
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Bluebird Bio Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- HemaQuest Pharmaceuticals Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Emmaus Medical Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Baxter International Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
- Prolong Pharmaceuticals
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
- Medunik USA Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
- Sangamo Therapeutics, Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
- Global Blood Therapeutics
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
- Alnylam Pharmaceuticals
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
- Acceleron Pharma, Inc.
  - Company Highlights
  - Product Portfolio
  - Key Highlights
  - Financial Performance
  - Market Strategies
Section
- Research Methodology
- About Us

*Browse 32 market data tables and 27 figures on “Hemoglobinopathy Treatment Drugs Market”- Global forecast to 2030

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