Table of Contents

1. Research Objectives and Assumptions
   • Research Objectives
   • Assumptions
   • Abbreviations
2. Market Purview
   • Report Description
     • Market Definition and Scope
   • Executive Summary
     • Market Fanconi Anemia Drug, By Treatment Type
     • Market Fanconi Anemia Drug, By Age Group
     • Market Fanconi Anemia Drug, By Disease Stage
     • Market Fanconi Anemia Drug, By Region
   • Coherent Opportunity Map (COM)
3. Market Dynamics, Regulations, and Trends Analysis
   • Market Dynamics
     • Drivers
       • Continuous advancements in scientific research and understanding of the molecular mechanisms
       • Substantial unmet medical need
     • Restraints
       • Lack of recognized therapies
     • Opportunities
       • Development of Disease-Modifying Therapies
   • Impact Analysis
   • Key Highlights
   • Regulatory Scenario
   • Product Launches/Approvals
   • PEST Analysis
   • PORTER’s Analysis
   • Merger and Acquisition Scenario
4. Global Fanconi Anemia Drug Market – Impact of Coronavirus (COVID-19) Pandemic
   • COVID-19 Epidemiology
   • Supply Side and Demand Side Analysis
   • Economic Impact
5. Global Fanconi Anemia Drug Market, By Treatment Type, 2018-2030, (US$ Mn)
   • Introduction
     • Market Share Analysis, 2023 and 2030 (%)
     • Y-o-Y Growth Analysis, 2019–2030
     • Segment Trends
   • Hematopoietic Growth Factors
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
   • Gene Therapy
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
   • Stem Cell Transplantation
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
   • Other Therapies
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
6. Global Fanconi Anemia Drug Market, By Age Group, 2018-2030, (US$ Mn)
   • Introduction
     • Market Share Analysis, 2023 and 2030 (%)
     • Y-o-Y Growth Analysis, 2019–2030
     • Segment Trends
   • Pediatric Patients
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
   •  Adult Patients
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
7. Global Fanconi Anemia Drug Market, By Disease Stage, 2018-2030, (US$ Mn)
   • Introduction
     • Market Share Analysis, 2023 and 2030 (%)
     • Y-o-Y Growth Analysis, 2019–2030
     • Segment Trends
   • Early-stage Disease
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
   • Advanced-stage Disease
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
8. Global Fanconi Anemia Drug Market, By Region, 2018-2030, (US$ Mn)
   • Introduction
     • Market Share Analysis, By Region, 2023 and 2030 (%)
     • Y-o-Y Growth Analysis, For Region, 2018 –2030
     • Country Trends
   • North America
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, By Treatment Type, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Age Group, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Disease Stage, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Country, 2018-2030,(US$ Mn)
       • U.S.
       • Canada
   • Latin America
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, By Treatment Type, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Age Group, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Disease Stage, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Country, 2018-2030,(US$ Mn)
       • Brazil
       • Argentina
       • Mexico
       • Rest of Latin America
   • Europe
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, By Treatment Type, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Age Group, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Disease Stage, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Country, 2018-2030,(US$ Mn)
       • Germany
       • U.K.
       • Spain
       • France
       • Italy
       • Russia
       • Rest of Europe
   • Asia Pacific
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, By Treatment Type, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Age Group, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Disease Stage, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Country, 2018-2030,(US$ Mn)
       • China
       • India
       • Japan
       • Australia
       • South Korea
       • ASEAN
       • Rest of Asia Pacific
   • Middle East
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, By Treatment Type, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Age Group, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Disease Stage, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Country, 2018-2030,(US$ Mn)
       • GCC
       • Israel
       • Rest of Middle East
   • Africa
     • Introduction
     • Market Size and Forecast, and Y-o-Y Growth, By Treatment Type, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Age Group, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Disease Stage, 2018-2030, (US$ Mn)
     • Market Size and Forecast, and Y-o-Y Growth, By Country, 2018-2030,(US$ Mn)
       • South Africa
       • North Africa
       • Central Africa
9. Competitive Landscape
   • Foresee Pharmaceuticals Co., Ltd.
     • Company Highlights
     • Product Portfolio
     • Key Developments
     • Financial Performance
     • Strategies
   • Rocket Pharmaceuticals Inc.
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Amgen
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Novartis AG
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Gilead Sciences, Inc. (Kite Pharma, Inc.)
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Celgene Corporation (Juno Therapeutics)
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Spark Therapeutics
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • UniQure N.V
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Bluebird Bio, Inc.
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • PTC Therapeutics
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Orchard Therapeutics Limited
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • GlaxoSmithKline Plc.
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Aurora Biopharma, Inc.
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Pfizer, Inc.
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Autolus Therapeutics
     • Company Highlights
     • Product Portfolio
     • Key Highlights
     • Financial Performance
     • Strategies
   • Analyst Views
10. Section
    • Research Methodology
    • About us

*Browse 35 market data tables and 30 figures on “Global Fanconi Anemia Drug Market” - Global forecast to 2030